Gene Therapy Research

$35,345
14%
Raised toward our $250,000 Goal
66 Donors
81
days left
Project ends on June 30, at 11:59 PM AEST
Project Owners

An update from the Taouk family

March 02, 2020

Dear friends,

 

We have some great news to share – after searching far and wide and interviewing many talented scientists, CMRI has officially appointed a postdoctoral researcher to join the team as Taouk Family Researcher!

 

They will officially start at CMRI in late March to begin researching PGAP1 mutations and devising a construct for a gene therapy. Although we can’t share their identity just yet, CMRI have told us how excited they are about the skills the researcher will bring to the team with their strong experience in genome analysis, gene screening and molecular biology.

 

Thank you so much again for your support. We have been overwhelmed by your generosity. Your gifts will help cover our researcher’s lab necessities like reagents, models and materials, and potentially help support an additional third year of work for them if we manage to raise enough funding.

 

We are so excited and looking forward to discovering if this research holds the key to a treatment for our girls.

 

The Taouk family

 

Thank you for your support

December 20, 2019

Dear friends,

 

We can’t thank you enough for your support. In 10 days, you have already helped raise nearly $5000 toward the world’s first-ever gene therapy research for PGAP1 mutation.

 

We wanted to say thank you, and to give you a few updates.

 

The University of Sydney has written a beautiful article about our story and what the research will make possible – you can read it here.

 

You might also have seen it shared on the University’s Facebook page. We would so appreciate if you could ‘like’ and share the post so that we can spread the word even further.

 

Our local paper, the Parramatta Advertiser, has also picked up the story – if you are a subscriber, you can read their version here.

 

On behalf of our whole family, we are so grateful for your generosity. We wish you a wonderful holiday season and look forward to updating you on the crowdfunding campaign’s progress in the new year.

 

The Taouk family

 

Our Crowdfunding Groups